Lizzy has Spinal Muscular Atrophy Type 1 and is a miracle! She has NEVER been able to stand, walk or sit(with out assistance). She is such an amazing child with.
Repligen licensed RG3039 in 2009 from Families of Spinal Muscular Atrophy (FSMA), a patient advocacy organization that funded and directed the preclinical development of RG3039 with an investment of more than $13 million.
The Spinal Muscular Atrophy (SMA) Communities “Bucket List”. April 28, 2012 By Vincent Gaynor Leave a Comment. The time has come to thank the many families and groups that &
A newborn baby's battle with spinal muscular atrophy inspired her parents to start a bucket list blog. HULIQ reports on Avery's Bucket List blog, a site that aims to spread awareness of Avery's illness, which progressively weakens muscle function.
Brooklyn, who has the genetic disease spinal muscular atrophy, has overcome great odds. / Kevin Pieper/The Baxter Bulletin Kelly Carter, a physical therapist at Child & Youth Pediatric Day Clinic, puts new leg braces on 2-year-old Brooklyn Marie Gould